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dna

Databasing and the promise of of orphan drug discovery

This past week marks at least three news stories touting the hope and promise of databases as tools supporting rare disease patients and orphan drug discovery. These events include ...
bens_friends

Building Rare Disease Communities, one disease at a time

When Ben Munoz had his own experience with rare disease in 2006 he decided to build an online support group for patients like himself. Since that time, Ben and his team have created ...

Do orphan drug exclusivity provisions reduce patient access to existing drugs?

Authors Murphy, Puwanant and Griggs in a recently published study in the Annals of Neurology journal posed this question. The authors suggest that while orphan drug incentives encourage ...
shirelogo_yellow

Shire to publish Rare Disease Impact Report

(Reprinted from Shire press release 11/19/2012) Shire plc (LSE: SHP, NASDAQ: SHPGY) today announced a new initiative – the Shire Rare Disease Impact Report – to research the health, ...
UK Dept of health

UK Department of Health provides summary of responses for rare diseases plan

In February of 2012 the European Council Recommendation on Rare Disease requested responses aimed at measures designed to combat rare disease in Europe. Last week, the council release ...
PXE international

Rare Disease Advocacy Group backs Research Challenge Contest for PXE

PXE International, an advocacy group promoting the research and support of individuals with pseudoxanthoma elasticum (PXE) has announced a research challenge on Innocentive.com. Specifically, ...

Is the orphan drug market too crowded?

In a recent article discussing the impact of the re-election of President Obama, author Matthew Herper considers the future of the drug industry. Herper specifically suggests that ...
Questcor

What happens to the market when an orphan drug designation is mistaken as an orphan drug approval

A recent article in the Motley Fool reveals the market consequences when stakeholders are confused between the terms orphan drug designation and orphan drug approval. Specifically, ...
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